Mutation-Based Therapy for Duchenne Muscular Dystrophy: Antisense Treatment Arrives in the Clinic.

نویسندگان

  • Elizabeth M McNally
  • Eugene J Wyatt
چکیده

Tom Adriaenssens, MD, PhD; Michael Joner, MD; Thea C. Godschalk, MSc; Nikesh Malik, MD; Fernando Alfonso, MD, PhD; Erion Xhepa, MD; Dries De Cock, MD; Kenichi Komukai, MD; Tomohisa Tada, MD; Javier Cuesta, MD; Vasile Sirbu, MD; Laurent J. Feldman, MD, PhD; Franz-Josef Neumann, MD; Alison H. Goodall, PhD; Ton Heestermans, MD; Ian Buysschaert, MD, PhD; Ota Hlinomaz, MD; Ann Belmans, MSc; Walter Desmet, MD; Jurrien M. ten Berg, MD, PhD; Anthony H. Gershlick, MD; Steffen Massberg, MD; Adnan Kastrati, MD; Giulio Guagliumi, MD; Robert A. Byrne, MB, BCh, PhD; on behalf of the Prevention of Late Stent Thrombosis by an Interdisciplinary Global European Effort (PRESTIGE) Investigators

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عنوان ژورنال:
  • Circulation

دوره 136 11  شماره 

صفحات  -

تاریخ انتشار 2017